Preclinical Gene Therapy Studies for Hemophilia Using Adenoviral Vectors
نویسندگان
چکیده
منابع مشابه
Adenoviral Vectors for Hemophilia Gene Therapy
Hemophilia is an inherited blood clotting disorder resulting from deficiency of blood coagulation factors. Current standard of care for hemophilia patients is frequent intravenous infusions of the missing coagulation factor. Gene therapy for hemophilia involves the introduction of a normal copy of the deficient coagulation factor gene thereby potentially offering a definitive cure for the bleed...
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ژورنال
عنوان ژورنال: Seminars in Thrombosis and Hemostasis
سال: 2004
ISSN: 0094-6176,1098-9064
DOI: 10.1055/s-2004-825631